Duchenne muscular dystrophy
A warm, plain-language guide for families - and a place to follow the new treatments being developed for Duchenne.
What is Duchenne, in plain language
Duchenne muscular dystrophy (DMD) is a rare genetic condition that affects how muscles work. It is caused by changes in the gene that makes dystrophin, a protein that helps keep muscle cells strong. Without enough of it, muscles weaken gradually over time. Duchenne is usually diagnosed in early childhood and is most common in boys.
Every family's experience is different. Care has come a long way, and a coordinated team - including neurology, cardiology, pulmonology, physical therapy, and others - can make a real difference in day-to-day life. Research into new Duchenne treatments is active and moving quickly - and that is what Alma Studies follows most closely.
Our focus is the science of what is coming: the pipeline of new and upcoming therapies being developed for Duchenne. We translate that progress into clear, honest language - we will not promise cures or trial spots, and we will never overstate what is known. We are here to keep you in the loop as new treatments advance.
Follow the science as it moves.
The main reason Alma Studies is here: to keep you updated on new Duchenne treatments in development — honestly, and only when there's real progress. We will not promise cures or trial spots; this keeps you informed and is not trial enrollment or medical advice.
Is there a Duchenne clinical trial for you in the US?
Pick a condition below — we'll walk through a few simple questions and check whether there is an active US clinical trial that might be a fit. This is informational and is not medical advice or a guarantee of enrollment.
A free gift for your family
The Duchenne family guide
Our plain-language Duchenne family guide — what it is, today's care, and the treatments in development, written for families. It's a one-time gift, yours to download free, no sign-up needed. (The ongoing relationship is the drug-development news above.)
Download the free family guide (PDF)This page is for general information only and is not medical advice. It does not offer diagnosis, treatment, or guaranteed access to clinical trials. Always talk with your own care team about decisions for you or your child.
For clinicians, biotech & researchers
Duchenne drug-development landscape report
We maintain an in-depth intelligence report on the Duchenne pipeline — the mechanisms in development, the companies and programs behind them, and where clinical progress stands. Request a copy and we'll send the full PDF to your inbox.